Medicines in Development for Neurological Disorders 2018 Report

PhRMA April 17, 2018

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Neurological disorders are a group of more than 1,000 conditions that affect the brain and nervous system. Together, these disorders impact an estimated 100 million Americans, nearly a third of the U.S. population. Although some are well known, such as Alzheimer’s disease, epilepsy, migraine headaches, multiple sclerosis and Parkinson’s disease, many are rare and affect a small number of patients. Of the more than 7,000 known rare diseases, about 360 of them are primarily neurological, including amyotrophic lateral sclerosis (ALS) and Huntington’s disease.

Today, biopharmaceutical research companies are developing 537 medicines for numerous, wide-ranging neurological disorders. There is hope on the horizon, as scientists are uncovering more about how the nervous system works at the molecular and genetic levels, driving the development of innovative treatments for several neurological disorders. Download the report to learn more.

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Pat had just turned 30 when he started to feel weakness in his arms and hands. He went to the doctor, who diagnosed Pat with amyotrophic lateral sclerosis (ALS.) Instead of sitting back and giving in to the disease, Pat decided to fight back, publicly. He started spreading awareness about his disease and working with local fundraisers. Eventually, his path led him to co-create one of the biggest philanthropic movements in social media history—the Ice Bucket Challenge—with his friend Pete Frates. Today, Pat continues his fight against ALS alongside researchers who won’t stop until they find a cure.